Research Article

Open Access
Vamorolone targets dual nuclear receptors to treat inflammation and dystrophic cardiomyopathy
View ORCID ProfileChristopher R Heier Correspondence email, Qing Yu, Alyson A Fiorillo, Christopher B Tully, Asya Tucker, Davi A Mazala, Kitipong Uaesoontrachoon, Sadish Srinivassane, Jesse M Damsker, Eric P Hoffman, Kanneboyina Nagaraju, Christopher F Spurney
Christopher R Heier
1Department of Genomics and Precision Medicine, George Washington University School of Medicine and Health Sciences, Washington, DC, USA
2Center for Genetic Medicine Research, Children's National Medical Center, Washington, DC, USA
Qing Yu
2Center for Genetic Medicine Research, Children's National Medical Center, Washington, DC, USA
Alyson A Fiorillo
1Department of Genomics and Precision Medicine, George Washington University School of Medicine and Health Sciences, Washington, DC, USA
2Center for Genetic Medicine Research, Children's National Medical Center, Washington, DC, USA
Christopher B Tully
2Center for Genetic Medicine Research, Children's National Medical Center, Washington, DC, USA
Asya Tucker
2Center for Genetic Medicine Research, Children's National Medical Center, Washington, DC, USA
Davi A Mazala
2Center for Genetic Medicine Research, Children's National Medical Center, Washington, DC, USA
Kitipong Uaesoontrachoon
3AGADA Biosciences Incorporated, Halifax, Nova Scotia, Canada
Sadish Srinivassane
3AGADA Biosciences Incorporated, Halifax, Nova Scotia, Canada
Jesse M Damsker
4ReveraGen BioPharma, Incorporated, Rockville, MD, USA
Eric P Hoffman
3AGADA Biosciences Incorporated, Halifax, Nova Scotia, Canada
4ReveraGen BioPharma, Incorporated, Rockville, MD, USA
5School of Pharmacy and Pharmaceutical Sciences, Binghamton University—State University of New York (SUNY), Binghamton, NY, USA
Kanneboyina Nagaraju
3AGADA Biosciences Incorporated, Halifax, Nova Scotia, Canada
4ReveraGen BioPharma, Incorporated, Rockville, MD, USA
5School of Pharmacy and Pharmaceutical Sciences, Binghamton University—State University of New York (SUNY), Binghamton, NY, USA
Christopher F Spurney
1Department of Genomics and Precision Medicine, George Washington University School of Medicine and Health Sciences, Washington, DC, USA
2Center for Genetic Medicine Research, Children's National Medical Center, Washington, DC, USA
6Division of Cardiology, Children's National Heart Institute, Children's National Medical Center, Washington, DC, USA
Published 11 February 2019. DOI: 10.26508/lsa.201800186

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Effects of nuclear receptor ligands in DMD
Christopher R Heier, Qing Yu, Alyson A Fiorillo, Christopher B Tully, Asya Tucker, Davi A Mazala, Kitipong Uaesoontrachoon, Sadish Srinivassane, Jesse M Damsker, Eric P Hoffman, Kanneboyina Nagaraju, Christopher F Spurney
Life Science Alliance Feb 2019, 2 (1) e201800186; DOI: 10.26508/lsa.201800186
Effects of nuclear receptor ligands in DMD
Christopher R Heier, Qing Yu, Alyson A Fiorillo, Christopher B Tully, Asya Tucker, Davi A Mazala, Kitipong Uaesoontrachoon, Sadish Srinivassane, Jesse M Damsker, Eric P Hoffman, Kanneboyina Nagaraju, Christopher F Spurney
Life Science Alliance Feb 2019, 2 (1) e201800186; DOI: 10.26508/lsa.201800186
In this Issue
Volume 2, No. 1
February 2019
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